An investigation to determine the efficacy and safety of lentivirus mediated FXN gene delivery
Funder: Ataxia UKDuration: March 2011 - February 2014
People
| Name | Telephone | Office | ||
|---|---|---|---|---|
|
Professor Michael Themis Professor - Gene Therapy and Genotoxicity (Principal investigator)
T: +44 (0)1895 267252
E: michael.themis@brunel.ac.uk |
+44 (0)1895 267252 | michael.themis@brunel.ac.uk | Heinz Wolff 235 |
Outputs
Khonsari, H., Schneider, M., Al-Mahdawi, S., Chianea, YG., Themis, M., Parris, C., et al. (2016) 'Lentivirus-meditated frataxin gene delivery reverses genome instability in Friedreich ataxia patient and mouse model fibroblasts'. Nature Gene Therapy, 23 (12). pp. 846 - 856. ISSN: 0969-7128 Open Access Link